2-Day Webinar: Global Hematological Rare Disease Alliance

Speakers include Professor Franco Locatelli (Italy) who will address Accessibility to Gene Therapy for Hemoglobinopathies in Europe, and Dr John F. Tisdale (USA) addressing Accessibility of Gene Therapy treatments in the US.

The GARDEN confronts rare hematological diseases, including both congenital and acquired blood disorders that affect Hematopoietic Stem Cells. These diseases, though relatively rare, pose significant challenges in terms of diagnosis, treatment, and scientific research, especially due to their rarity and the limited investment in their study. As of 2015, there were 296 different definitions of rare diseases worldwide, with sub-Saharan Africa having high incidences of Sickle Cell Disease (SCD), for instance…