A New Day for People with Sickle Cell Disease

Earlier this month, President Trump took to his Truth Social, lambasting Leticia James for dragging her feet on sickle cell, while linking to a Roger Stone Substack on the issue.

During his remarks in Charleston remarks, Kennedy noted that South Carolina, which has a high number of citizens affected by sickle cell disease, has “helped inform the design of our model.”

Kennedy specifically thanked South Carolina Senator Tim Scott for being a “long and loud advocate and champion for people with sickle cell disease.” He also expressed appreciation to other states that have joined the effort. “The success of this model shows that voluntary approaches can work when you have the right partners across the table,” Kennedy said.

One of the right partners is Patrick Girondi, founder of San Rocco Therapeutics, who said his company’s new therapeutic gene therapy will be more effective and significantly less expensive than other therapies currently on the market.

Girondi, whose son has thalassemia, an inherited blood disorder, created Rocco Therapeutics to make treatments for rare diseases more available and less expensive for those afflicted.