Researcher Pioneers Faster, Cheaper Gene Therapy for Hemoglobin Disorders

For millions living with hemoglobin deficiencies such as sickle cell disease or beta thalassemia, every day is a battle against pain, costly treatments, and uncertainty. Dr. Frank Park is racing to help. A new gene therapy being developed at the University of Tennessee Health Science Center could provide a more accessible cure. Frank Park, PhD, a researcher at UT Health Sciences’ College of Pharmacy, believes he’s on the verge of a more efficient and affordable solution that could revolutionize how we combat hemoglobin deficiencies through his gene therapy, nicknamed “Minirolu.”

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