SRT at ASGCT | Abstract 3507

SRT at ASGCT | Abstract 3507

SRT at ASGCT | Abstract 3507 3507 A lentiviral vector with enhanced titer and T87Q β-globin expression for treatment of severe β-hemoglobin disorders   INTRODUCTIONSickle cell disease (SCD) and β-thalassemia are caused by defect or deficiency in adult β-globin....
SRT at ASGCT | Abstract 465

SRT at ASGCT | Abstract 465

SRT at ASGCT | Abstract 465 465 A RT-qPCR assay for precise detection and absolute quantification of the T87Q β-globin variant in erythroid progeny of lentivirus transduced human CD34+ cells   INTRODUCTIONLentiviral vectors (LVV) encoding for erythroid-specific...